Therapies database

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Regeneron Pharmaceuticals · Gene Therapy · Approved
ApprovedTherapeuticStronger sources
Population
Children & adults · FDA label has no age bounds; trial: 10 months–16 years
Biallelic OTOF severe-to-profound deafness
Evidence
regulatory
Confidence
99%
Indications
Hearing LossSensorineural Hearing LossGenetic Hearing LossOTOF-Related Hearing Loss
Details
Regeneron Pharmaceuticals · Drug Delivery · Phase 1
CompletedTherapeutic
Population
Adults · ≥18 years
Cancer patients receiving high-dose cisplatin
Evidence
publication
Confidence
92%
Indications
Cisplatin-Induced Hearing LossHearing Loss
Details

A listing is not proof of safety or effectiveness. Approval and availability may vary by indication and country.

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