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Program Map

Start with a treatment, device, company, diagnosis, or trial ID. Each record keeps the source trail close to the claim.

161Main(26 active)
148Status checked
135Strong
320Backlog
More filters and sort (1 active)
7 records in Main database · 4 strong · 5 status checked
Regeneron Pharmaceuticals · Gene Therapy · Approved
ApprovedTherapeuticStronger sources
Evidence
regulatory
Confidence
99%
Indications
Hearing LossSensorineural Hearing LossGenetic Hearing LossOTOF-Related Hearing Loss
Population
PediatricAdultCongenitalGenetic
Details
Eli Lilly and Company · Gene Therapy · Phase 2
ActiveTherapeuticStronger sources
Evidence
trial
Confidence
95%
Indications
Hearing LossSensorineural Hearing LossGenetic Hearing LossOTOF-Related Hearing Loss
Population
PediatricAdultCongenitalGenetic
Details
Sensorion · Gene Therapy · Phase 1/2
ActiveTherapeuticStronger sources
Evidence
trial
Confidence
94%
Indications
Hearing LossSensorineural Hearing LossGenetic Hearing LossOTOF-Related Hearing Loss
Population
PediatricCongenitalGeneticOTOF / DFNB9
Details
Sensorion · Gene Therapy · Preclinical
ActiveTherapeuticStronger sources
Evidence
company
Confidence
88%
Indications
Hearing LossSensorineural Hearing LossGenetic Hearing Loss
Population
CongenitalGeneticPre-Lingual
Details
Otonomy · Gene Therapy · Preclinical
DiscontinuedTherapeutic
Evidence
company
Confidence
87%
Indications
Hearing LossSensorineural Hearing LossGenetic Hearing Loss
Population
PediatricCongenitalGeneticPre-Lingual
Details
Shanghai EuHearing Therapeutics Co., Ltd · Gene Therapy · Phase 1/2
ActiveTherapeutic
Evidence
trial
Confidence
90%
Indications
Hearing LossSensorineural Hearing LossGenetic Hearing LossOTOF-Related Hearing Loss
Population
PediatricGeneticCongenitalOTOF / DFNB9
Details
OtoVia Therapeutics · Gene Therapy · Interventional/NA
UnknownTherapeutic
Evidence
registry+publication
Confidence
86%
Indications
Hearing LossSensorineural Hearing LossGenetic Hearing LossDFNB9
Population
PediatricAdultGeneticDfnb9
Details