Therapeutics
Details checkedClinical trial listing onlyCheckedregistry

Investigator-sponsored rilonacept study for autoimmune neurosensory hearing loss

Also known as: Rilonacept, Arcalyst, IL-1 Trap

Investigator-sponsored study (Stanley Cohen, MD)

Primary source
Sponsor / Institution
Investigator-sponsored study (Stanley Cohen, MD)
Program Type
Therapeutic
Modality
Biologic
Stage
Early Phase 1
Status
Unknown
Target Gene
Route / Mode
Subcutaneous injection
Confidence
78%
Status Confidence
Status needs checking
Evidence Strength
Needs more support
Last Reviewed
2026-06-09
Geography
United States
Population
adult, older-adult, autoimmune-inner-ear-disease, progressive, bilateral
Trial IDs
1
Mechanism

Subcutaneous interleukin-1 blocker/cytokine trap. The Arcalyst label describes rilonacept as binding IL-1 alpha and IL-1 beta as a soluble decoy receptor, while the hearing study tested whether IL-1 blockade could improve autoimmune neurosensory hearing loss.

Indications
Notes

Verified as a real open-label investigator-sponsored pilot study of rilonacept/Arcalyst in autoimmune neurosensory hearing loss. ClinicalTrials.gov lists Stanley Cohen, MD as sponsor-investigator with Metroplex Clinical Research affiliation and Regeneron Pharmaceuticals as an industry collaborator; this should not be represented as a Regeneron hearing-loss pipeline program. The ClinicalTrials.gov record remains Unknown with last-known Recruiting status, has not been updated since September 2017, and has no posted results. DailyMed currently lists Arcalyst/rilonacept under Kiniksa labeling and confirms the IL-1 blocker mechanism and subcutaneous route, but the approved indications are not hearing-loss indications.

Evidence & Sources
2 structured sources
clinicaltrials
Supports: canonicalName, aliases, company, allCompanies, isIndustrySponsored, indications, stage, status...
IDs: NCT02828033, Rilonacept IIS 1604, Rilonacept, Arcalyst, IL-1 Trap
Open
drug label
Supports: aliases, modality, mechanism, route, allCompanies, notes
IDs: Arcalyst, rilonacept, Kiniksa Pharmaceuticals (UK), Ltd., Regeneron Pharmaceuticals, Inc.
Open
Key Events
Clinical Trials (1)
Data Checks
investigator-sponsored-not-company-pipelineregistry-only-current-statusno-public-results-confirmedstatus-unknown-after-estimated-completionnot-approved-for-hearing-loss
Related Programs