Therapeutics
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Colorado SLOS Cholesterol and Antioxidant Study

Also known as: Cholesterol and Antioxidant Treatment in Patients With Smith-Lemli-Opitz Syndrome (SLOS), Cholesterol and Antioxidant Treatment in Patients With Smith-Lemli-Opitz Syndrome, DEKAS Plus antioxidant arm, cholesterol suspension / eggs / Slo-lesterol arm, Smith-Lemli-Opitz syndrome cholesterol antioxidant study, NCT01773278

Institution-led study

Primary source
Sponsor / Institution
Institution-led study
Program Type
Therapeutic
Modality
Small Molecule
Stage
Phase 2
Status
Unknown
Target Gene
DHCR7
Route / Mode
Oral/dietary cholesterol supplementation and oral antioxidant supplementation
Confidence
84%
Status Confidence
Status needs checking
Evidence Strength
Needs more support
Last Reviewed
2026-06-10
Geography
United States
Population
genetic, syndromic, pediatric, adult, hearing-monitoring
Trial IDs
1
Mechanism

Academic Phase 2 study treating biochemically confirmed Smith-Lemli-Opitz syndrome with cholesterol supplementation plus antioxidant medication, while monitoring sterol biochemistry and serial clinical measures including brainstem audiometry. Hearing loss is part of the syndromic phenotype and monitoring plan, but the cholesterol and antioxidant components are one systemic SLOS treatment protocol rather than separate hearing-loss pipeline programs.

Indications
Notes

Promoted as a verified registry-backed academic SLOS treatment-protocol record while preserving the stale-status caveat. ClinicalTrials.gov and registry mirrors describe one University of Colorado study treating Smith-Lemli-Opitz syndrome with cholesterol supplementation and antioxidant medication, with hearing monitored as part of the syndromic phenotype; these protocol components should not appear as separate hearing-loss pipeline programs.

Evidence & Sources
3 structured sources
clinicaltrials
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IDs: NCT01773278
Open
registry mirror
Supports: canonicalName, aliases, stage, route, populationTags, notes
IDs: NCT01773278
Open
registry mirror
Supports: canonicalName, aliases, stage, route, notes
IDs: NCT01773278
Open
Key Events
Clinical Trials (1)
Data Checks
institution-led-studymerged-generated-intervention-armsstudy-level-not-standalone-productsyndromic-hearing-loss-adjacentregistry-only-evidenceregistry-status-date-inconsistencycurrent-status-not-verified
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