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Compare up to 6 HearScape records side by side across ownership, modality, stage, evidence, populations, trials, source support, and review notes.

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FieldOtarmeni by Regeneron
Regeneron Pharmaceuticals
OrganizationCompany: Regeneron Pharmaceuticals
Program TypeTherapeutic
ModalityGene Therapy
Stage / StatusApproved / Approved
Review Statuschecked · regulatory
Confidence99%
Target / GeneOTOF
Route / ModeIntracochlear infusion
IndicationsHearing Loss; Sensorineural Hearing Loss; Genetic Hearing Loss; OTOF-Related Hearing Loss; Auditory Neuropathy
Population Tagspediatric; adult; congenital; genetic; otof-dfnb9; pre-lingual; bilateral; profound
GeographyUnited States; European Union; United Kingdom; Spain
Trials
Source Support3 structured sources · 3 URL-backed · regulatory, company, clinicaltrials
Last Reviewed2026-05-31
Data ChecksNo data flags
MechanismDual-AAV intracochlear gene replacement delivers functional OTOF to cochlear inner hair cells to restore otoferlin-mediated auditory signaling.
NotesField-defining OTOF program; transitioned from Decibel to Regeneron after the 2023 acquisition and became the first approved gene therapy for genetic hearing loss in 2026.